NIH Muscular Dystrophy Research Task Force Agenda
One Democracy Plaza
6701 Democracy Blvd., Suite 800
Bethesda, MD 20817
TEL: 301-594-5055
“Promoting Treatment”
January 21, 2003
7:00 - 9:00 p.m.
| 7:00 PM | Welcome and Introductions |
| 7:30 PM | Meeting Goals |
| 8:00 PM | Review of Thursday Agenda |
| 8:30 PM | Discussion of Goals and Topics |
| 9:00 PM | Adjourn |
January 22, 2003
8:30 a.m. - 3:00 p.m.
| 8:30 AM | Review Agenda | |
| 8:45 AM | Treatments for Muscular Dystrophy | |
| Symptoms being treated | Introduction: Dr. Craig M. McDonald | |
| Target Tissues and Organs | Introduction: Dr. Elizabeth McNally | |
| Outcome goals | Introduction: Dr. Charles A. Thornton | |
| Outcome measures | Introduction: Dr. Craig M. McDonald | |
| 10:15 AM | NIH Office of Rare Diseases - Promoting Treatment Dr. Stephen Groft |
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| 10:45 AM | FDA Office of Orphan Products Development - Orphan Drug Development Dr. John McCormick |
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| 11:15 AM | MDA - Activities Promoting Treatment Development Dr. Sharon Hesterlee Dr. Rodney Howell |
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| 11:45 AM | NIH Translation Research Initiatives Dr. Robert Baughman |
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| 12:00 PM | Lunch | |
| 12:15 PM | Survey of Potential Therapies Introduction: Dr. Louis Kunkel | |
| 12:45 PM | Identifying Priority Areas Recruitment Strategy for Study Participants |
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| 1:30 PM | Promoting cooperation by NIH, Federal agencies, health voluntary groups, and industry | |
| 2:30 PM | Summarize | |
| 3:00 PM | Adjourn | |